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Therapeutic options for CTLA-4 insufficiency

113 Citations2021
David Egg, Ina Caroline Rump, Noriko Mitsuiki

Systemic immunosuppressants and abatacept may provide partial control but require ongoing administration and allogeneic hematopoietic stem cell transplantation offers a possible cure for patients with CTLA-4 insufficiency.

Abstract

Systemic immunosuppressants and abatacept may provide partial control but require ongoing administration. Allogeneic hematopoietic stem cell transplantation offers a possible cure for patients with CTLA-4 insufficiency.

Therapeutic options for CTLA-4 insufficiency